An Under-the-radar Trailblazer

Engineering breakthroughs for some of the world’s most brutal genetic disorders.

Wall Street’s darlings chase billion-dollar blockbusters.

This company?

It’s on a different mission entirely—one most investors will miss until it’s too late.

Tucked away in a niche most of biotech avoids, this under-the-radar trailblazer is engineering breakthroughs for some of the world’s most brutal genetic disorders. Not someday. Now.

With a pipeline …